Duchenne Muscular Dystrophy Clinical Symposium

On Friday, August 26, 2016, UT Southwestern's Wellstone Muscular Dystrophy Center hosted the first annual Duchenne Muscular Dystrophy Clinical Symposium.

There were two goals of the Symposium:

  • Provide an overview of genome editing and its potential application for treating DMD patients.
  • Provide DMD patients and their families with a comprehensive overview of the clinical approach to caring for DMD patients.


Welcome Message and Introduction

Gene Editing: An Innovative Therapy for DMD by Eric N. Olson, Ph.D.

Disease in a Dish: Precision Medicine and Permanent Gene Correction by Myoediting by Jay W. Schneider, M.D., Ph.D.

Clinical Trials and DMD by Jerry Mendell, M.D.

DMD Associated Cardiomyopathy by Pradeep P.A. Mammen, M.D.

Pulmonary Management of DMD/BMD by Peter N. Schochet, M.D.

Lifestyle Recommendations and Exercise and Muscle Pain by Christopher Flores, R.D., L.D., and Leslie Nelson, P.T., M.P.T., O.C.S.

Panel Discussion