The UT Southwestern Wellstone Center will tackle two main scientific projects, along with patient education and student training.

• Project 1 seeks to correct muscular dystrophy in a mouse model of Duchenne muscular dystrophy using a gene-editing technique developed at UT Southwestern called Myoediting.
• Project 2 will use blood cells from Duchenne muscular dystrophy patients to create stem cells, called induced pluripotent stem cells (iPSCs), which can be used for Myoediting to delete the DMD mutation in the patient’s cells. 

The goal of the UTSW Wellstone Center is to eventually take potential therapies developed from this gene-editing technique to human clinical trials.