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Novel Therapeutics

  • Next-Generation RNA Therapeutics for Polycystic Kidney Disease
  • Avidity-Based Therapeutics for Protein Misfolding Disorders such as Alzheimer’s
  • Drugging ADP-Ribosylation Pathways in Cancer and Neurodegeneration
  • siRNA Therapeutics for Renal Cell Carcinoma
  • Bleb-Septin Signaling as a Therapeutic Target in Metastatic Cancer
  • Precision Viral Delivery Targeting Metastatic Cancer
  • Small-Molecule Modulators of Circadian Biology
  • Hormone-Sensing Virulence Blockers for Staphylococcus aureus
  • Forward Genetic Screens for Next-Generation Immunotherapies
  • Molecular Therapeutics for Heterotopic Ossification
  • Next-Generation CAR-T Therapies for Solid Tumors
  • Ribo-SNAP Technology to Control Ribosome Biogenesis to treat cancer and aging
  • Mitochondrial Import Pathways: TOMM as a Therapeutic Frontier
  • Patient-Derived Antibody Therapeutics for Neurodegeneration
  • ASObiotic Precision Antibiotics for Drug-Resistant Infections
  • Targeting Orm2–IL23R Signaling for Next-Generation IBD Therapy
  • Targeting Stress-Induced tRNA Fragments (tiRNAs) for Next-Generation Therapeutics
  • Immune Modulator Therapeutics for Nerve Regeneration
  • Inherently Antimicrobial Bone Cement for Orthopedic Infections
  • Microbiome-Derived Immunotherapies for Cancer and Autoimmune Disease